Hemophilia. After a setback, gene therapy progresses...gingerly

Science. 2001 Mar 2;291(5509):1692-7. doi: 10.1126/science.291.5509.1692.
No abstract available

Publication types

  • News

MeSH terms

  • Animals
  • Clinical Trials as Topic*
  • Dependovirus / genetics
  • Dogs
  • Factor IX / genetics
  • Factor VIII / genetics
  • Genetic Research*
  • Genetic Therapy* / adverse effects
  • Genetic Vectors / administration & dosage
  • Hemophilia A / genetics
  • Hemophilia A / therapy
  • Hemophilia B / genetics
  • Hemophilia B / therapy*
  • Humans
  • Liver / metabolism
  • Muscles / metabolism
  • United States
  • United States Food and Drug Administration

Substances

  • Factor VIII
  • Factor IX